Utilizing Innovative Statistical Methods and Trial Designs in Rare Disease Drug Development

Event Date:



Convened by the Duke-Robert J. Margolis, MD, Center for Health Policy at Duke University and supported by a cooperative agreement with FDA, this public event will bring the stakeholder community together to discuss the challenges that rare disease settings pose for treatment development and regulatory decision-making, as well as the promising study designs and analytical methods that can help overcome them.



Starting Time:

9:00 am

Ending Time:

5:00 pm